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ASGCT 2020 Annual Meeting
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Gene Therapy for Inborn Errors of Metabolism: New Approaches
WEBINAR ENDED
Friday, May 15, 2020 · 10:15 a.m.
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· 2 hours
Gene Therapy for Inborn Errors of Metabolism: New Approaches
Friday, May 15, 2020 · 10:15 a.m. · Eastern Time (US & Canada)
Who can view:
Everyone
Webinar Price:
Free
Featured Presenters
Cary Harding
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Petr Ilyinskii
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Stefanos Koutsoukos
The first viable mouse model of combined methylmalonic acidemia and homocystinuria, cblC type displays a sustained response to a single dose of AAV gene therapy and is comparable to chronic hydroxocobalamin administration
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Lili Wang
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Suhail Khoja
Dr.
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Shunji Tomatsu
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Vivek Chowdhary
Post-Doc Associate
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Mark Osborn
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Hosted By
ASGCT 23rd Annual Meeting
The full session archive, available exclusively for attendees of the American Society of Gene & Cell Therapy's 23rd Annual Meeting, May 12-15, 2020.
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